Latest gene therapy News

Mutated bone stem cells caught in a loop leading to osteogenesis imperfecta type V
C3i Center Inc is First CDMO in Canada to Receive Approval for a Drug Establishment License to Commercially Produce Cell Therapy Drug Products
Groundbreaking cancer treatment may trigger more cancer – but here’s why you shouldn’t worry
Recipients of CIMED project grants and clinical research months 2025-2027
When there’s no commercial incentive to develop gene therapy – hospitals will try to fill the gap
No commercial incentive to develop gene therapy – hospitals will try to fill the gap
Orthoptists At Heart Of Vision Research
‘Cloaked’ proteins deliver cancer-killing therapeutics into cells
ACTION Centre to boost access to life-saving new therapies for children
New sickle cell disease drug approved for use in England – here’s how voxelotor works
CAR T cell therapy targeting HER2 antigen shows promise against advanced sarcoma in phase I trial
Pioneering Research Wins Prestigious EU Funding
Ride Raising Money And Awareness To Save Sight
Expanding Newborn Screening For Victorian Babies
Global Search For Missing Glaucoma Link
New company established to operate NSW’s world-leading viral vector facility
UQ health and medical research secures $10.2 million boost
CSL reports strong first half growth with immunoglobulins the highlight
Inherited retinal disease carriers need more support
How does HIV get into the cell’s centre to kickstart infection?
CAR T cell therapy for T cell lymphoma shows promise in phase I trial
A novel switch to turn genes on/off, promising step toward safer gene therapy
Research aims to transform haemophilia treatment
Centenary researchers awarded more than $2m in Ideas Grants
The Cell and Gene Catalyst call for change in submission to scope of practice review
AstraZeneca announces collaboration and investment agreement with Cellectis to accelerate cell therapy and genomic medicine ambitions
Groundbreaking gene therapy trial for Hunter syndrome opens
Dan L Duncan Comprehensive Cancer Center to open cell therapy clinical trials at Harris Health
COVID proved the therapeutic potential of RNA technology – making it more available is the next goal
Life changing gene therapy for babies with spinal muscular atrophy
Viralgen welcomes back Andy Holt as CCO
New view of gene therapy
Research: DNA shredder for gene therapy
Oculus BioMed partners with The Centre for Eye Research Australia in a deal to develop ‘SwitchGene’
CSL announces seven new Global Research Acceleration Initiative projects
Viralgen Vector Core and Elpida Therapeutics partner to manufacture gene therapy medicines for anticipated Spastic Paraplegia 50 (SPG50) and Charcot-Marie-Tooth disease type…
Next stop: retina
Alexion completes purchase and licence agreement for early-stage rare disease gene therapy portfolio from Pfizer
CSL reports strong profit growth with record plasma collections
How a cat got people talking about rare neurological diseases
Alexion, AstraZeneca Rare Disease, enters agreement with Pfizer to acquire a portfolio of preclinical rare disease gene therapies
Gene Therapy Treats Chronic Pain by Dialing Down Sodium
World first trial for kids with Duchenne Muscular Dystrophy
NSW new world first trial for kids with Duchenne Muscular Dystrophy
RNA – changing face of modern medicine
Gene therapy could help fight glaucoma: discovery
RNA offers hope for new Parkinson’s treatment
See future: Annual Review 2022